Capricor Therapeutics Publishes Peer-Reviewed Study About Deramiocel Cell Therapy
Capricor Therapeutics announced the publication in Biomedicines, an international peer-reviewed journal, describing a novel in-vitro potency assay designed to characterize the anti-fibrotic mechanism of...
REGENXBIO Announces Completion of RGX-202 Pivotal Enrollment and Initiates Commercial Production in Duchenne Gene Therapy Program
REGENXBIO announced the completion of enrollment in the AFFINITY DUCHENNE pivotal trial of RGX-202, an investigational gene therapy for the treatment of Duchenne muscular...
Hansa’ Imlifidase Reduce Anti-AAV Antibodies and Allow Administration of Gene Therapy
SRP-9001-104 in Duchenne muscular dystrophy (DMD): Topline results were reported for three patients with DMD treated with imlifidase prior to administration of Sarepta's ELEVIDYS...
Avidity Biosciences to be Acquired by Novartis
Avidity Biosciences, which is developing an exon 44 skipping therapy for Duchenne muscular dystrophy, announced that it has entered into a definitive merger agreement...
A Statement from NorthStar Network on Givinostat (Duvyzat)
According to an announcement on the Muscular Dystrophy UK website, NorthStar Network stated: 'As part of ongoing surveillance of the risk profile of Givinostat...