Approved Therapies

EMA Recommends EU Approval for Duvyzat (givinostat) to Treat Duchenne Muscular Dystrophy

The European Medicines Agency (EMA) has suggested that Duvyzat (givinostat) be given a conditional marketing authorization in the EU to treat Duchenne muscular dystrophy...

NICE Final Guidance for AGAMREE (Vamorolone) as a Treatment for Duchenne Muscular Dystrophy Is Positive for Santhera

AGAMREE (vamorolone) has been recommended for use in the National Health Service (NHS) in England, Wales, and Northern Ireland for the treatment of Duchenne...

Vamorolone (Agamree) Approved in Scotland

The medication vamorolone, also marketed under the brand name Agamree, has been approved by the Scottish Medicines Consortium (SMC) as a therapy option for...

What is Agamree (vamorolone)? What is Agamree Used For?

We will answer your questions such as what is AGAMREE (Vamorolone), which is used in the treatment of Duchenne Muscular Dystrophy (DMD) and is...

Frequently Asked Questions About Eteplirsen (Exondys 51) for DMD Treatment

Let's learn together the answers to the frequently asked questions by Duchenne muscular dystrophy (DMD) patients about Eteplirsen (Exondys 51), which was approved by...

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