Duchenne Muscular Dystrophy (DMD) Exon 51 Skipping Therapies: A Promising Cures and Clinical Trials
Duchenne Exon 51 skipping therapies are innovative treatments aimed at addressing the genetic mutation responsible for Duchenne muscular dystrophy (DMD). By skipping exon 51...
Shanghai Jiao Tong University School of Medicine Begins Clinical Trials of LE051 Exon 51 Skipping Therapy
The purpose of LE051 study is to evaluate the safety, tolerability, and efficacy of LE051 intravenous therapy in DMD patients treated with exon 51...
Fn14 Protein May Protect Muscle Stem Cells, Offering Promise for Development of Duchenne Treatments
For millions of people, losing muscle means losing their freedom as well as their strength. Muscle loss, whether from Duchenne muscular dystrophy, aging, or...
Significant Improvements Seen in 3 Children Receiving Dystrogen Therapeutics’ DT-DEC01 Cell Therapy
In non-ambulatory individuals with Duchenne muscular dystrophy (DMD), DT-DEC01 (Dystrogen Therapeutics), an experimental dystrophin expressing chimeric (DEC) cell treatment, was found to be safe...
Researchers in Madrid Make Important Strides in the Cure of Duchenne Muscular Dystrophy with Nanoparticles
The Community of Madrid has achieved significant progress in therapy for Duchenne muscular dystrophy, a degenerative disease for which there is still no cure....