News on Approved Treatments for Duchenne Muscular Dystrophy (DMD)

About us

We do not want children to die from a disease that can be cured. We want to give hope to families and ensure that all children with DMD are treated and regain their health.

Latest Articles

ImmunoForge Receives FDA IND Approval for Phase 2 Clinical Trial of ‘Pemziviptadil’ for DMD Cardiomyopathy

Research January 14, 2025 0

A medication for DMD cardiomyopathy, pemziviptadil is used once...

Sarepta Reiterated Total Net Product Revenue of $3.0 Billion in 2025

DMD January 14, 2025 0

As children and families battling Duchenne Muscular Dystrophy wait...

Wave Life Sciences Announces Plans for Exon 53 Skipping Study in 2025

DMD January 14, 2025 0

Alpha-1 antitrypsin deficiency (AATD), Huntington's disease (HD), obesity, and...

Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy

DMD December 26, 2024 1

A genetic condition known as Duchenne muscular dystrophy (DMD)...

Capricor Therapeutics Submits Application for Treatment of DMD Cardiomyopathy

Research October 10, 2024 0

Capricor Therapeutics, a biotechnology company developing transformative cell and...

Cures of Duchenne (List of All Researches)

Research September 20, 2024 3

Dystrophin Gene Therapy MechanismCompanyDrugStatus Micro-dystrophin Gene Replacement Sarepta TherapeuticsElevidys/SRP-9001ApprovedMicro-dystrophin Gene ReplacementPfizerPF-06939926DiscontinuedMicro-dystrophin Gene...

Approved Treatments

What is Agamree (vamorolone)? What is Agamree Used For?

Frequently Asked Questions About Eteplirsen (Exondys 51) for DMD Treatment

UK Approves Givinostat (Duvyzat) for Duchenne Muscular Dystrophy Treatment

Santhera Announces Approval in Hong Kong for AGAMREE® (Vamorolone) as a Treatment for Duchenne Muscular Dystrophy

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