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Home
Categories
DMD
Research
Press Releases
Approved Treatments
Editorials
Family Stories
Cures
WhatsApp Channel
About Us
Contact
More
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Precision BioSciences Highlights New Preclinical Data for PBGENE-DMD for the Treatment of Duchenne Muscular Dystrophy
Press Releases
DMD Warrior
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Precision BioSciences a clinical stage gene editing company utilizing its novel proprietary ARCUS® platform to develop in vivo gene...
Vyondys 53: What Does FDA Rejection Letter Mean?
Editorials
DMD Warrior
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The Food and Drug Administration published more than 200 letters it sent to companies after their medications were rejected...
Sarepta Therapeutics Halts ELEVIDYS Shipments for Non-Ambulatory DMD Patients
Press Releases
DMD Warrior
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Due to two documented incidents of severe liver failure that resulted in death, Sarepta Therapeutics has stopped shipping its...
Medera and University of Kansas Medical Center Announce First Patient Treated in Pioneering Gene Therapy Trial (SRD-001) for Duchenne Muscular Dystrophy Associated Cardiomyopathy
Research
DMD Warrior
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Mutations Amenable to Exon 50 Skipping Therapies in Duchenne Muscular Dystrophy
DMD
DMD Warrior
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BBM-D101 Gene Therapy Phase 1/2 Clinical Trial Begins
Research
DMD Warrior
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JCR Pharmaceuticals Proprietary JUST-AAV Capsids May be Used in the Development of Duchenne Cures
Press Releases
DMD Warrior
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