Solid Biosciences Provides Update on INSPIRE DUCHENNE Clinical Trial Progress and Planned Regulatory Discussions
Solid Biosciences announced positive new interim data from the Phase 1/2 INSPIRE DUCHENNE clinical trial. The Company also provided an update to the planned...
Five-Year Data of AGAMREE (vamorolone) in Patients with DMD Show Improved Safety Profile with Comparable Effectiveness to Standard of Care Corticosteroids
Santhera reported positive topline results from an analysis of long-term data, including first assessments from the ongoing, open-label, multicenter GUARDIAN study evaluating AGAMREE (vamorolone)...
Capricor Therapeutics Publishes Peer-Reviewed Study About Deramiocel Cell Therapy
Capricor Therapeutics announced the publication in Biomedicines, an international peer-reviewed journal, describing a novel in-vitro potency assay designed to characterize the anti-fibrotic mechanism of...
REGENXBIO Announces Completion of RGX-202 Pivotal Enrollment and Initiates Commercial Production in Duchenne Gene Therapy Program
REGENXBIO announced the completion of enrollment in the AFFINITY DUCHENNE pivotal trial of RGX-202, an investigational gene therapy for the treatment of Duchenne muscular...
Hansa’ Imlifidase Reduce Anti-AAV Antibodies and Allow Administration of Gene Therapy
SRP-9001-104 in Duchenne muscular dystrophy (DMD): Topline results were reported for three patients with DMD treated with imlifidase prior to administration of Sarepta's ELEVIDYS...