Preclinical Study: Cell Therapy Prevents Damage From Duchenne Muscular Dystrophy
A cell therapy preserves muscle structure and function in laboratory mice with a type of disease similar to Duchenne muscular dystrophy, according to new...
Genethon to Launch Pivotal Trial in Europe of GNT0004 a Low-Dose Microdystrophin Gene Therapy for Duchenne Muscular Dystrophy
Genethon has received approvals from regulatory authorities, MHRA and EMA, to begin pivotal Phase 3 clinical trials in France and the UK of its...
UW Medicine Announces New Gene Therapy Research for Duchenne Muscular Dystrophy
For those who suffer from Duchenne muscular dystrophy (DMD), a novel gene therapy holds promise for both stopping muscle loss and maybe restoring the...
INS1201 Gene Therapy Phase 1 Clinical Trial Begins
Insmed was announced on the page published on ClinicalTrials.gov with the ID NCT06817382 that the phase 1 trials of INS1201 gene therapy developed for...
Medera and University of Kansas Medical Center Announce First Patient Treated in Pioneering Gene Therapy Trial (SRD-001) for Duchenne Muscular Dystrophy Associated Cardiomyopathy
Medera a clinical-stage biopharmaceutical company focused on targeting cardiovascular diseases by developing next-generation therapeutics, and its clinical development division Sardocor, together with the University...