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Press Releases
Ractigen Therapeutics Reports Positive First-in-Human Data for RAG-18 in Duchenne
Press Releases
GEN6050X Exon 50 Skipping Base Editing Drug: One-Year Results Show Encouraging Progress for Duchenne Muscular Dystrophy
Research
China-Based Ractigen Therapeutics is Initiating Clinical Trials to Investigate The Safety and Tolerability of RAG-18 in Patients with DMD
RAG-18
Research
Ractigen Therapeutics Doses First Patient in IIT Study of RAG-18, a Potential Game-Changing saRNA Therapeutic for Duchenne Muscular Dystrophy
Research
SPOT-mRNA03 Gene Therapy for Duchenne Muscular Dystrophy Begins Early Phase 1 Clinical Trial
Press Releases
Belief BioMed Announced Successful Completion of First Dose of BBM-D101 Gene Therapy
Research
BBM-D101 Gene Therapy Phase 1/2 Clinical Trial Begins
Press Releases
Belief BioMed BBM-D101 Gene Therapy Receives IND Clearance by National Medical Products Administration (NMPA)
Research
Shanghai Jiao Tong University School of Medicine Begins Clinical Trials of LE051 Exon 51 Skipping Therapy
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Frequently Asked Questions About Elevidys Used for DMD
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August 21, 2026
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Press Releases
GEN6050X Exon 50 Skipping Base Editing Drug: One-Year Results Show Encouraging Progress for Duchenne Muscular Dystrophy
Research
Sarcomatrix Plans First Human Trial of S-969 for Duchenne Muscular Dystrophy in 2027
Editorials
7 Breakthrough DMD Research Programs That Could Transform Duchenne Treatment in 2026