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Research
PBGENE-DMD Enters Clinical Trials: First Patient Dosed in Duchenne Gene-Editing Study
Research
Precision BioSciences Announced the Start of Phase 1/2a (FUNCTION-DMD) Study of PBGENE-DMD in Ambulatory Patients with Duchenne
Press Releases
Satellos Announces First Participant Dosed in Phase 2 Pediatric Study of SAT-3247 for Duchenne Muscular Dystrophy
Press Releases
Entrada Therapeutics Announced It will Report Data from its Exon Skipping Studies in 2026
Research
Satellos Announced the Start of Phase 2A (BASECAMP) Study of SAT-3247 in Ambulatory Patients with Duchenne
Research
China-Based Ractigen Therapeutics is Initiating Clinical Trials to Investigate The Safety and Tolerability of RAG-18 in Patients with DMD
RAG-18
Press Releases
Satellos Announces First Adult Patient Dosed in LT-001, an Open-Label, Long-Term Follow-Up Study of SAT-3247 in Duchenne Muscular Dystrophy
Research
WVE-N531 Exon Skipping Therapy Phase 2 Clinical Trial Begins for Duchenne Muscular Dystrophy
Research
SPOT-mRNA03 Gene Therapy for Duchenne Muscular Dystrophy Begins Early Phase 1 Clinical Trial
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Care Guidelines
Breathing Exercises in Duchenne Muscular Dystrophy: Respiratory Therapy, Pulmonary Care & Lung Support
Research
BioMarin Launches BMN 351 Exon 51 Skipping Therapy Phase 2 Clinical Trial for Duchenne Muscular Dystrophy
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