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Duchenne MD
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Press Releases
Belief BioMed Announced Successful Completion of First Dose of BBM-D101 Gene Therapy
Research
Solid Biosciences Initiates Phase 3 Clinical Trial of SGT-003 Gene Therapy (IMPACT DUCHENNE) in Ambulant Males
Research
Entrada Therapeutics Begins Clinical Trials in Europe for Exon 44 and Exon 45 Skipping Therapies
Press Releases
Edgewise Therapeutics Reports Positive Results on Sevasemten Program for Becker and Duchenne Muscular Dystrophies
Press Releases
PepGen Announces It Will Halt Clinical Trials of Exon 51 Skipping Study
Research
Satellos Prepares to Launch Phase 2 Clinical Study of SAT-3247 for the Treatment of Duchenne Muscular Dystrophy
Press Releases
Three Ongoing Clinical Trials of Elevidys Gene Therapy Temporarily Halted in Europe
Research
Russian Biotech Company Generium has Begun Clinical Trials of a Gene Therapy for Duchenne Muscular Dystrophy
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Frequently Asked Questions About Elevidys Used for DMD
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August 21, 2026
Must Read
Research
Del-Zota SAFARI44 Phase 3 Trial: A New Exon 44 Skipping Study for Duchenne Muscular Dystrophy
Press Releases
RGX-202 Duchenne Gene Therapy Shows NSAA Improvement and Microdystrophin Expression — But Important Biomarker Data Missing
Editorials
CRISPR GuideX Tool: hfCas12Max in CRISPR-Based Therapeutics
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