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Duchenne MD
What is Duchenne?
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Latest Posts
Editorials
The Systemic Failure of DMD Associations: Why Duchenne Patients Are Still Waiting
Editorials
In Which Countries Is Elevidys Approved? Is Elevidys Approved In Europe?
Press Releases
Exegenesis Bio and Modalis Collaborate to Advance MDL-201 for Duchenne Muscular Dystrophy
Articles by:
Can Ekinci
Press Releases
Sarepta Therapeutics Halts ELEVIDYS Shipments for Non-Ambulatory DMD Patients
Research
Medera and University of Kansas Medical Center Announce First Patient Treated in Pioneering Gene Therapy Trial (SRD-001) for Duchenne Muscular Dystrophy Associated Cardiomyopathy
Research
BBM-D101 Gene Therapy Phase 1/2 Clinical Trial Begins
Press Releases
JCR Pharmaceuticals Proprietary JUST-AAV Capsids May be Used in the Development of Duchenne Cures
Press Releases
Taiho Pharmaceutical Announced TAS-205 Phase 3 Clinical Study Did Not Meet Its Primary Endpoint
Editorials
Accredited Duchenne Centers (ADC) Aims to Provide Uniform and Up-to-date Care for All People Living with Duchenne Muscular Dystrophy
Research
RGX-202 Gene Therapy Phase 3 Clinical Trial Begins
Research
Entrada Therapeutics Begins Clinical Trials in Europe for Exon 44 and Exon 45 Skipping Therapies
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Latest Posts
Editorials
The Systemic Failure of DMD Associations: Why Duchenne Patients Are Still Waiting
Editorials
In Which Countries Is Elevidys Approved? Is Elevidys Approved In Europe?
Press Releases
Exegenesis Bio and Modalis Collaborate to Advance MDL-201 for Duchenne Muscular Dystrophy
Research
Tevard’s tRNA Therapy Targets Nonsense Mutations to Restore Full-Length Dystrophin in DMD
Don't Miss
Press Releases
Elixirgen and Nippon Shinyaku Partner on Full-Length Dystrophin Therapy for Duchenne
Press Releases
REGENXBIO Completes RGX-202 Confirmatory Study for Duchenne Muscular Dystrophy
Care Guidelines
DMD Circumcision Guide: Safety Precautions, Anesthesia, and Aftercare
Editorials
If Elevidys Works for Duchenne Muscular Dystrophy, Why Is Sarepta’s Stock Falling? What Families Need to Know Before Choosing Gene Therapy
Press Releases
GEn1E Lifesciences and GEn-1123: A New Precision Medicine Approach for Duchenne Muscular Dystrophy (DMD)
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