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Duchenne MD
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Latest Posts
Press Releases
Deramiocel Shows Positive 24-Month HOPE-3 Results in Duchenne
Press Releases
Ractigen Therapeutics Reports Positive First-in-Human Data for RAG-18 in Duchenne
Press Releases
Entrada Therapeutics’ ENTR-601-44 Shows Dose-Dependent Exon 44 Skipping in Early PK/PD Data
Articles by:
Can Ekinci
Research
Capricor Therapeutics Submits Application for Treatment of DMD Cardiomyopathy
Research
Satellos Produced Near-Normal Levels of Dystrophin in Experiment with Dogs with DMD with SAT-3247
Research
CRISPR-Cas13 Could Accelerate Studies on RNA-Targeted Therapies
Research
New Gene Therapy Study at Indiana University Offers Hope for Duchenne Muscular Dystrophy
Family Stories
The Story of Aziz, DMD Warrior from Turkey
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Latest Posts
Press Releases
Deramiocel Shows Positive 24-Month HOPE-3 Results in Duchenne
Press Releases
Ractigen Therapeutics Reports Positive First-in-Human Data for RAG-18 in Duchenne
Press Releases
Entrada Therapeutics’ ENTR-601-44 Shows Dose-Dependent Exon 44 Skipping in Early PK/PD Data
Press Releases
NS Pharma’s Brogidirsen Shows 5-Year Clinical Data in DMD Patients Amenable to Exon 44 Skipping
Don't Miss
Press Releases
GEN6050X Exon 50 Skipping Base Editing Drug: One-Year Results Show Encouraging Progress for Duchenne Muscular Dystrophy
Research
Sarcomatrix Plans First Human Trial of S-969 for Duchenne Muscular Dystrophy in 2027
Editorials
7 Breakthrough DMD Research Programs That Could Transform Duchenne Treatment in 2026
Press Releases
Dyne Therapeutics Announces U.S. FDA Acceptance of Biologics License Application (BLA) for Z-Rostudirsen, an Exon 51 Skipping Therapy for Duchenne Muscular Dystrophy (DMD)
Press Releases
Santhera Expands Biomedica Agreement to Extend AGAMREE (Vamorolone) Distribution Across Central Asia and the Caucasus
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