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Latest Posts
Press Releases
GEN6050X Exon 50 Skipping Base Editing Drug: One-Year Results Show Encouraging Progress for Duchenne Muscular Dystrophy
Research
Sarcomatrix Plans First Human Trial of S-969 for Duchenne Muscular Dystrophy in 2027
Editorials
7 Breakthrough DMD Research Programs That Could Transform Duchenne Treatment in 2026
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DMD Warrior
Press Releases
Edgewise Therapeutics Reports Positive Results on Sevasemten Program for Becker and Duchenne Muscular Dystrophies
Press Releases
Precision BioSciences Receives FDA Rare Pediatric Disease Designation for PBGENE-DMD for the Treatment of Duchenne Muscular Dystrophy
Press Releases
Capricor Therapeutics Provides Regulatory Update on Deramiocel BLA for Duchenne Muscular Dystrophy
Press Releases
Cumberland’s Ifetroban Demonstrated a 5.4% Improvement Compared to Placebo-Treated Patients
Approved Therapies
What is Duvyzat (Givinostat)?
Press Releases
Capricor Therapeutics Announces Positive 4-Year Data of Deramiocel (CAP-1002) in Duchenne Muscular Dystrophy
Editorials
After Second Patient Death, Duchenne Muscular Dystrophy Communities Want Answers About Elevidys Gene Therapy
Press Releases
Capricor Therapeutics Announces BMD Orphan Drug Designation and DMD Program Regulatory Development for Deramiocel (CAP-1002)
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Latest Posts
Press Releases
GEN6050X Exon 50 Skipping Base Editing Drug: One-Year Results Show Encouraging Progress for Duchenne Muscular Dystrophy
Research
Sarcomatrix Plans First Human Trial of S-969 for Duchenne Muscular Dystrophy in 2027
Editorials
7 Breakthrough DMD Research Programs That Could Transform Duchenne Treatment in 2026
Press Releases
Dyne Therapeutics Announces U.S. FDA Acceptance of Biologics License Application (BLA) for Z-Rostudirsen, an Exon 51 Skipping Therapy for Duchenne Muscular Dystrophy (DMD)
Don't Miss
DMD
Dystrophin Gene in Duchenne Muscular Dystrophy: Function, Mutations & Treatments
Care Guidelines
Constipation in Duchenne Muscular Dystrophy: Causes, Symptoms & Treatment
Care Guidelines
Calcium in Duchenne Muscular Dystrophy: Mechanisms, Risks, and Treatment Insights
Editorials
Why CK, AST, and ALT Data Matter More Than Videos in Duchenne Gene Therapy
DMD
Does My Child Have Duchenne Muscular Dystrophy (DMD)?
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