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Duchenne MD
What is Duchenne?
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Latest Posts
Editorials
The Systemic Failure of DMD Associations: Why Duchenne Patients Are Still Waiting
Editorials
In Which Countries Is Elevidys Approved? Is Elevidys Approved In Europe?
Press Releases
Exegenesis Bio and Modalis Collaborate to Advance MDL-201 for Duchenne Muscular Dystrophy
Articles by:
Can Ekinci
Press Releases
Capricor Therapeutics Announces BMD Orphan Drug Designation and DMD Program Regulatory Development for Deramiocel (CAP-1002)
Press Releases
Sarepta Reported Elevidys Gene Therapy for Duchenne Muscular Dystrophy will not be used in non-ambulatory patients
ELEVIDYS
Approved Therapies
European Commission Approves Duvyzat for the Treatment of Duchenne Muscular Dystrophy
Press Releases
New Positive Functional Data From The RGX-202 Affinity Duchenne® Trial Phase 1/2 Reported By Regenxbio
Regenxbio RGX-202
Press Releases
PepGen Announces It Will Halt Clinical Trials of Exon 51 Skipping Study
Press Releases
Entrada Therapeutics Receives EU Authorization to Start Exon 45 Skipping Clinical Trial in Duchenne Muscular Dystrophy
Press Releases
Entos Pharmaceuticals Develops Re-Dosable, Full-Length Dystrophin Gene Therapy: Fusogenix PLV Method
Press Releases
Genethon Reports Results of GNT0004 Gene Therapy Clinical Trial: Permanent Decrease in CK Levels of More Than 75%
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Latest Posts
Editorials
The Systemic Failure of DMD Associations: Why Duchenne Patients Are Still Waiting
Editorials
In Which Countries Is Elevidys Approved? Is Elevidys Approved In Europe?
Press Releases
Exegenesis Bio and Modalis Collaborate to Advance MDL-201 for Duchenne Muscular Dystrophy
Research
Tevard’s tRNA Therapy Targets Nonsense Mutations to Restore Full-Length Dystrophin in DMD
Don't Miss
Press Releases
Elixirgen and Nippon Shinyaku Partner on Full-Length Dystrophin Therapy for Duchenne
Press Releases
REGENXBIO Completes RGX-202 Confirmatory Study for Duchenne Muscular Dystrophy
Care Guidelines
DMD Circumcision Guide: Safety Precautions, Anesthesia, and Aftercare
Editorials
If Elevidys Works for Duchenne Muscular Dystrophy, Why Is Sarepta’s Stock Falling? What Families Need to Know Before Choosing Gene Therapy
Press Releases
GEn1E Lifesciences and GEn-1123: A New Precision Medicine Approach for Duchenne Muscular Dystrophy (DMD)
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