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Latest Posts
Research
DYNE-251 Phase 3 FORZETTO Clinical Trial of Z-Rostudirsen Officially Begins for DMD
Care Guidelines
What Is a Spirometry Test in Duchenne Muscular Dystrophy (DMD) and Why Is It Performed?
Care Guidelines
Age-Based Assistive Devices for Duchenne Muscular Dystrophy: Complete Guide by Stage
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DMD Warrior
Research
RGX-202 Gene Therapy Phase 3 Clinical Trial Begins
Research
Entrada Therapeutics Begins Clinical Trials in Europe for Exon 44 and Exon 45 Skipping Therapies
Editorials
Wellcome Trust Donates £10 Million to Treat Rare Diseases
Press Releases
Edgewise Therapeutics Reports Positive Results on Sevasemten Program for Becker and Duchenne Muscular Dystrophies
Press Releases
Precision BioSciences Receives FDA Rare Pediatric Disease Designation for PBGENE-DMD for the Treatment of Duchenne Muscular Dystrophy
Press Releases
Capricor Therapeutics Provides Regulatory Update on Deramiocel BLA for Duchenne Muscular Dystrophy
Press Releases
Cumberland’s Ifetroban Demonstrated a 5.4% Improvement Compared to Placebo-Treated Patients
Approved Therapies
What is Duvyzat (Givinostat)?
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Latest Posts
Research
DYNE-251 Phase 3 FORZETTO Clinical Trial of Z-Rostudirsen Officially Begins for DMD
Care Guidelines
What Is a Spirometry Test in Duchenne Muscular Dystrophy (DMD) and Why Is It Performed?
Care Guidelines
Age-Based Assistive Devices for Duchenne Muscular Dystrophy: Complete Guide by Stage
Research
Del-Zota SAFARI44 Phase 3 Trial: A New Exon 44 Skipping Study for Duchenne Muscular Dystrophy
Don't Miss
DMD
Investigational New Drug (IND) Clearance for Duchenne Muscular Dystrophy: Process, Trials & Future Therapies
Editorials
Potential Upcoming New Gene Therapies for Duchenne Muscular Dystrophy
Care Guidelines
Hydrotherapy in Duchenne Muscular Dystrophy (DMD): Benefits, Exercises, and Clinical Evidence
Care Guidelines
Newly Diagnosed Patients with Duchenne Muscular Dystrophy: A Complete Family Guide
Press Releases
New Hope for Duchenne: Ryoncil Clinical Trial Begins
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