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Latest Posts
Research
Sarcomatrix Plans First Human Trial of S-969 for Duchenne Muscular Dystrophy in 2027
Editorials
7 Breakthrough DMD Research Programs That Could Transform Duchenne Treatment in 2026
Press Releases
Dyne Therapeutics Announces U.S. FDA Acceptance of Biologics License Application (BLA) for Z-Rostudirsen, an Exon 51 Skipping Therapy for Duchenne Muscular Dystrophy (DMD)
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DMD Warrior
Press Releases
FDA Investigating Death of 8-Year-Old Brazilian Boy Who Received Elevidys
Press Releases
The European Medicines Agency (EMA) Issued a Negative Opinion on Elevidys
Press Releases
Brazil Suspends Use of ELEVIDYS (delandistrogene moxeparvovec)
DMD
Mutations and Deletions Amenable to Exon 44 Skipping Therapies for Duchenne Muscular Dystrophy
Press Releases
FDA Designates Avidity Biosciences’ Delpacibart Zotadirsen (del-zota) as a Breakthrough Therapy for the Treatment of DMD in Individuals with Mutations That Allow for Exon...
Editorials
Roche Suspends Shipments of Elevidys Gene Therapy Outside of the United States
Press Releases
The FDA Designates PBGENE-DMD as an Orphan Drug by Precision BioSciences to Treat Duchenne Muscular Dystrophy
Press Releases
Sarepta Therapeutics Announces Pause of ELEVIDYS Shipments in the USA
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Latest Posts
Research
Sarcomatrix Plans First Human Trial of S-969 for Duchenne Muscular Dystrophy in 2027
Editorials
7 Breakthrough DMD Research Programs That Could Transform Duchenne Treatment in 2026
Press Releases
Dyne Therapeutics Announces U.S. FDA Acceptance of Biologics License Application (BLA) for Z-Rostudirsen, an Exon 51 Skipping Therapy for Duchenne Muscular Dystrophy (DMD)
Press Releases
Santhera Expands Biomedica Agreement to Extend AGAMREE (Vamorolone) Distribution Across Central Asia and the Caucasus
Don't Miss
Care Guidelines
Constipation in Duchenne Muscular Dystrophy: Causes, Symptoms & Treatment
Care Guidelines
Calcium in Duchenne Muscular Dystrophy: Mechanisms, Risks, and Treatment Insights
Editorials
Why CK, AST, and ALT Data Matter More Than Videos in Duchenne Gene Therapy
DMD
Does My Child Have Duchenne Muscular Dystrophy (DMD)?
Research
ELEVIDYS ENHANCE Study: A Phase 4 Trial Begins to Evaluate Safety and Effectiveness in Duchenne Muscular Dystrophy
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