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Latest Posts
Research
Sarcomatrix Plans First Human Trial of S-969 for Duchenne Muscular Dystrophy in 2027
Editorials
7 Breakthrough DMD Research Programs That Could Transform Duchenne Treatment in 2026
Press Releases
Dyne Therapeutics Announces U.S. FDA Acceptance of Biologics License Application (BLA) for Z-Rostudirsen, an Exon 51 Skipping Therapy for Duchenne Muscular Dystrophy (DMD)
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DMD Warrior
Research
Revidia Therapeutics MSI-1436 Holds Promise for Treating Heart Failure in DMD Patients
Press Releases
Keros Therapeutics Focuses on Advancing KER-065 for Duchenne Muscular Dystrophy (DMD)
Research
Preclinical Study: Cell Therapy Prevents Damage From Duchenne Muscular Dystrophy
Press Releases
Dyne Therapeutics Announces FDA Breakthrough Therapy Designation for DYNE-251 in Duchenne Muscular Dystrophy (DMD)
Press Releases
High Anti-AAV Antibodies May No Longer Be a Barrier to Elevidys Administration
Press Releases
MetrioPharm’s MP1032 Receives EMA Orphan Drug Designation in Duchenne Muscular Dystrophy
Research
Genethon to Launch Pivotal Trial in Europe of GNT0004 a Low-Dose Microdystrophin Gene Therapy for Duchenne Muscular Dystrophy
Press Releases
FDA: ‘Elevidys Gene Therapy Will Continue to Be Used in Ambulatory DMD Patients’
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Latest Posts
Research
Sarcomatrix Plans First Human Trial of S-969 for Duchenne Muscular Dystrophy in 2027
Editorials
7 Breakthrough DMD Research Programs That Could Transform Duchenne Treatment in 2026
Press Releases
Dyne Therapeutics Announces U.S. FDA Acceptance of Biologics License Application (BLA) for Z-Rostudirsen, an Exon 51 Skipping Therapy for Duchenne Muscular Dystrophy (DMD)
Press Releases
Santhera Expands Biomedica Agreement to Extend AGAMREE (Vamorolone) Distribution Across Central Asia and the Caucasus
Don't Miss
Care Guidelines
Constipation in Duchenne Muscular Dystrophy: Causes, Symptoms & Treatment
Care Guidelines
Calcium in Duchenne Muscular Dystrophy: Mechanisms, Risks, and Treatment Insights
Editorials
Why CK, AST, and ALT Data Matter More Than Videos in Duchenne Gene Therapy
DMD
Does My Child Have Duchenne Muscular Dystrophy (DMD)?
Research
ELEVIDYS ENHANCE Study: A Phase 4 Trial Begins to Evaluate Safety and Effectiveness in Duchenne Muscular Dystrophy
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