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Latest Posts
Editorials
7 Breakthrough DMD Research Programs That Could Transform Duchenne Treatment in 2026
Press Releases
Dyne Therapeutics Announces U.S. FDA Acceptance of Biologics License Application (BLA) for Z-Rostudirsen, an Exon 51 Skipping Therapy for Duchenne Muscular Dystrophy (DMD)
Press Releases
Santhera Expands Biomedica Agreement to Extend AGAMREE (Vamorolone) Distribution Across Central Asia and the Caucasus
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DMD Warrior
Press Releases
Solid Biosciences Announces 2026 Outlook for Clinical Trials of Duchenne Gene Therapy SGT-003
Press Releases
Edgewise Therapeutics Shared its Priorities for Becker and Duchenne Muscular Dystrophy in 2026
Press Releases
Precision BioSciences Anticipates Beginning Patient Dosing for Duchenne Muscular Dystrophy in The Early Second Quarter of 2026
Press Releases
Entrada Therapeutics Announced It will Report Data from its Exon Skipping Studies in 2026
Press Releases
Nxera Pharma Licenses Japan and Select Asia-Pacific Rights to Vamorolone for Duchenne Muscular Dystrophy from Santhera Pharmaceuticals
Editorials
‘One-Time’ Gene Therapies or Exon-Skipping Therapies: Which May Be Better for Duchenne’s Disease Today?
Press Releases
Italfarmaco and JCR Pharmaceuticals Announce Commercialisation Agreement for Duvyzat (Givinostat) in Japan and Strategic Collaboration in Rare Disease
Research
Satellos Announced the Start of Phase 2A (BASECAMP) Study of SAT-3247 in Ambulatory Patients with Duchenne
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Latest Posts
Editorials
7 Breakthrough DMD Research Programs That Could Transform Duchenne Treatment in 2026
Press Releases
Dyne Therapeutics Announces U.S. FDA Acceptance of Biologics License Application (BLA) for Z-Rostudirsen, an Exon 51 Skipping Therapy for Duchenne Muscular Dystrophy (DMD)
Press Releases
Santhera Expands Biomedica Agreement to Extend AGAMREE (Vamorolone) Distribution Across Central Asia and the Caucasus
DMD
Creatine Kinase Level in Duchenne Muscular Dystrophy: Normal Ranges, High CK Levels, Diagnosis, Blood Tests & FAQs
Don't Miss
Care Guidelines
Calcium in Duchenne Muscular Dystrophy: Mechanisms, Risks, and Treatment Insights
Editorials
Why CK, AST, and ALT Data Matter More Than Videos in Duchenne Gene Therapy
DMD
Does My Child Have Duchenne Muscular Dystrophy (DMD)?
Research
ELEVIDYS ENHANCE Study: A Phase 4 Trial Begins to Evaluate Safety and Effectiveness in Duchenne Muscular Dystrophy
Care Guidelines
Guide to DMD for Parents and Teachers at School: A Complete Guide for Safety, Learning, Friendship and Inclusion
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