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Duchenne MD
What is Duchenne?
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Latest Posts
Editorials
The Systemic Failure of DMD Associations: Why Duchenne Patients Are Still Waiting
Editorials
In Which Countries Is Elevidys Approved? Is Elevidys Approved In Europe?
Press Releases
Exegenesis Bio and Modalis Collaborate to Advance MDL-201 for Duchenne Muscular Dystrophy
Articles by:
Can Ekinci
Press Releases
Precision BioSciences Anticipates Beginning Patient Dosing for Duchenne Muscular Dystrophy in The Early Second Quarter of 2026
Press Releases
Entrada Therapeutics Announced It will Report Data from its Exon Skipping Studies in 2026
Press Releases
Nxera Pharma Licenses Japan and Select Asia-Pacific Rights to Vamorolone for Duchenne Muscular Dystrophy from Santhera Pharmaceuticals
Editorials
‘One-Time’ Gene Therapies or Exon-Skipping Therapies: Which May Be Better for Duchenne’s Disease Today?
Press Releases
Italfarmaco and JCR Pharmaceuticals Announce Commercialisation Agreement for Duvyzat (Givinostat) in Japan and Strategic Collaboration in Rare Disease
Research
Satellos Announced the Start of Phase 2A (BASECAMP) Study of SAT-3247 in Ambulatory Patients with Duchenne
Press Releases
Secretary Kennedy Expands Newborn Screening to Include Duchenne Muscular Dystrophy in USA
Research
China-Based Ractigen Therapeutics is Initiating Clinical Trials to Investigate The Safety and Tolerability of RAG-18 in Patients with DMD
RAG-18
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Latest Posts
Editorials
The Systemic Failure of DMD Associations: Why Duchenne Patients Are Still Waiting
Editorials
In Which Countries Is Elevidys Approved? Is Elevidys Approved In Europe?
Press Releases
Exegenesis Bio and Modalis Collaborate to Advance MDL-201 for Duchenne Muscular Dystrophy
Research
Tevard’s tRNA Therapy Targets Nonsense Mutations to Restore Full-Length Dystrophin in DMD
Don't Miss
Press Releases
Elixirgen and Nippon Shinyaku Partner on Full-Length Dystrophin Therapy for Duchenne
Press Releases
REGENXBIO Completes RGX-202 Confirmatory Study for Duchenne Muscular Dystrophy
Care Guidelines
DMD Circumcision Guide: Safety Precautions, Anesthesia, and Aftercare
Editorials
If Elevidys Works for Duchenne Muscular Dystrophy, Why Is Sarepta’s Stock Falling? What Families Need to Know Before Choosing Gene Therapy
Press Releases
GEn1E Lifesciences and GEn-1123: A New Precision Medicine Approach for Duchenne Muscular Dystrophy (DMD)
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