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Duchenne MD
What is Duchenne?
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Latest Posts
Editorials
The Systemic Failure of DMD Associations: Why Duchenne Patients Are Still Waiting
Editorials
In Which Countries Is Elevidys Approved? Is Elevidys Approved In Europe?
Press Releases
Exegenesis Bio and Modalis Collaborate to Advance MDL-201 for Duchenne Muscular Dystrophy
Articles by:
Can Ekinci
Research
Ractigen Therapeutics Doses First Patient in IIT Study of RAG-18, a Potential Game-Changing saRNA Therapeutic for Duchenne Muscular Dystrophy
Press Releases
Atossa Therapeutics Receives FDA Rare Pediatric Disease Designation for (Z)-Endoxifen for Duchenne Muscular Dystrophy
Press Releases
Satellos Receives FDA and International Clearance to Commence Pediatric Phase 2 Testing of SAT-3247 for Duchenne Muscular Dystrophy
Press Releases
Dyne Therapeutics to Apply for Accelerated Approval in Q2 2026 for Exon 51 Skipping Therapy (DYNE-251)
Press Releases
Capricor Therapeutics Announces Positive Topline Results from Pivotal Phase 3 HOPE-3 Study of Deramiocel in Duchenne Muscular Dystrophy
Press Releases
Del-Zota Clinical Trial Begins in the US in Participants with DMD Mutations Amenable to Exon 44 Skipping
Research
Researchers Develop Optimized Smad7 Gene Therapy to Target Duchenne Muscular Dystrophy
Press Releases
ELEVIDYS Gene Therapy for Non-Ambulant Children with DMD: FDA OKs ENDEAVOR Cohort 8 Immunosuppression Study
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Latest Posts
Editorials
The Systemic Failure of DMD Associations: Why Duchenne Patients Are Still Waiting
Editorials
In Which Countries Is Elevidys Approved? Is Elevidys Approved In Europe?
Press Releases
Exegenesis Bio and Modalis Collaborate to Advance MDL-201 for Duchenne Muscular Dystrophy
Research
Tevard’s tRNA Therapy Targets Nonsense Mutations to Restore Full-Length Dystrophin in DMD
Don't Miss
Press Releases
Elixirgen and Nippon Shinyaku Partner on Full-Length Dystrophin Therapy for Duchenne
Press Releases
REGENXBIO Completes RGX-202 Confirmatory Study for Duchenne Muscular Dystrophy
Care Guidelines
DMD Circumcision Guide: Safety Precautions, Anesthesia, and Aftercare
Editorials
If Elevidys Works for Duchenne Muscular Dystrophy, Why Is Sarepta’s Stock Falling? What Families Need to Know Before Choosing Gene Therapy
Press Releases
GEn1E Lifesciences and GEn-1123: A New Precision Medicine Approach for Duchenne Muscular Dystrophy (DMD)
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