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Latest Posts
Research
DYNE-251 Phase 3 FORZETTO Clinical Trial of Z-Rostudirsen Officially Begins for DMD
Care Guidelines
What Is a Spirometry Test in Duchenne Muscular Dystrophy (DMD) and Why Is It Performed?
Care Guidelines
Age-Based Assistive Devices for Duchenne Muscular Dystrophy: Complete Guide by Stage
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DMD Warrior
Editorials
Six DMD Researches You Should Follow up in 2026
Editorials
‘One-Time’ Gene Therapies or Exon-Skipping Therapies: Which May Be Better for Duchenne’s Disease Today?
Press Releases
Italfarmaco and JCR Pharmaceuticals Announce Commercialisation Agreement for Duvyzat (Givinostat) in Japan and Strategic Collaboration in Rare Disease
Research
Satellos Announced the Start of Phase 2A (BASECAMP) Study of SAT-3247 in Ambulatory Patients with Duchenne
Press Releases
Secretary Kennedy Expands Newborn Screening to Include Duchenne Muscular Dystrophy in USA
Research
China-Based Ractigen Therapeutics is Initiating Clinical Trials to Investigate The Safety and Tolerability of RAG-18 in Patients with DMD
RAG-18
Research
Ractigen Therapeutics Doses First Patient in IIT Study of RAG-18, a Potential Game-Changing saRNA Therapeutic for Duchenne Muscular Dystrophy
Press Releases
Atossa Therapeutics Receives FDA Rare Pediatric Disease Designation for (Z)-Endoxifen for Duchenne Muscular Dystrophy
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Latest Posts
Research
DYNE-251 Phase 3 FORZETTO Clinical Trial of Z-Rostudirsen Officially Begins for DMD
Care Guidelines
What Is a Spirometry Test in Duchenne Muscular Dystrophy (DMD) and Why Is It Performed?
Care Guidelines
Age-Based Assistive Devices for Duchenne Muscular Dystrophy: Complete Guide by Stage
Research
Del-Zota SAFARI44 Phase 3 Trial: A New Exon 44 Skipping Study for Duchenne Muscular Dystrophy
Don't Miss
DMD
Investigational New Drug (IND) Clearance for Duchenne Muscular Dystrophy: Process, Trials & Future Therapies
Editorials
Potential Upcoming New Gene Therapies for Duchenne Muscular Dystrophy
Care Guidelines
Hydrotherapy in Duchenne Muscular Dystrophy (DMD): Benefits, Exercises, and Clinical Evidence
Care Guidelines
Newly Diagnosed Patients with Duchenne Muscular Dystrophy: A Complete Family Guide
Press Releases
New Hope for Duchenne: Ryoncil Clinical Trial Begins
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