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Duchenne MD
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Latest Posts
Press Releases
Deramiocel Shows Positive 24-Month HOPE-3 Results in Duchenne
Press Releases
Ractigen Therapeutics Reports Positive First-in-Human Data for RAG-18 in Duchenne
Press Releases
Entrada Therapeutics’ ENTR-601-44 Shows Dose-Dependent Exon 44 Skipping in Early PK/PD Data
Articles by:
Can Ekinci
Press Releases
Elixirgen and Nippon Shinyaku Partner on Full-Length Dystrophin Therapy for Duchenne
Press Releases
REGENXBIO Completes RGX-202 Confirmatory Study for Duchenne Muscular Dystrophy
Care Guidelines
DMD Circumcision Guide: Safety Precautions, Anesthesia, and Aftercare
Editorials
If Elevidys Works for Duchenne Muscular Dystrophy, Why Is Sarepta’s Stock Falling? What Families Need to Know Before Choosing Gene Therapy
Press Releases
GEn1E Lifesciences and GEn-1123: A New Precision Medicine Approach for Duchenne Muscular Dystrophy (DMD)
Care Guidelines
Pain Management in Duchenne Muscular Dystrophy: A Parent’s Guide to Helping Your Child Live More Comfortably
Research
DYNE-251 Phase 3 FORZETTO Clinical Trial of Z-Rostudirsen Officially Begins for DMD
Care Guidelines
What Is a Spirometry Test in Duchenne Muscular Dystrophy (DMD) and Why Is It Performed?
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Latest Posts
Press Releases
Deramiocel Shows Positive 24-Month HOPE-3 Results in Duchenne
Press Releases
Ractigen Therapeutics Reports Positive First-in-Human Data for RAG-18 in Duchenne
Press Releases
Entrada Therapeutics’ ENTR-601-44 Shows Dose-Dependent Exon 44 Skipping in Early PK/PD Data
Press Releases
NS Pharma’s Brogidirsen Shows 5-Year Clinical Data in DMD Patients Amenable to Exon 44 Skipping
Don't Miss
Press Releases
GEN6050X Exon 50 Skipping Base Editing Drug: One-Year Results Show Encouraging Progress for Duchenne Muscular Dystrophy
Research
Sarcomatrix Plans First Human Trial of S-969 for Duchenne Muscular Dystrophy in 2027
Editorials
7 Breakthrough DMD Research Programs That Could Transform Duchenne Treatment in 2026
Press Releases
Dyne Therapeutics Announces U.S. FDA Acceptance of Biologics License Application (BLA) for Z-Rostudirsen, an Exon 51 Skipping Therapy for Duchenne Muscular Dystrophy (DMD)
Press Releases
Santhera Expands Biomedica Agreement to Extend AGAMREE (Vamorolone) Distribution Across Central Asia and the Caucasus
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