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Duchenne Muscular Dystrophy
Duchenne Muscular Dystrophy
Press Releases
Edgewise Therapeutics Reports Positive Results on Sevasemten Program for Becker and Duchenne Muscular Dystrophies
Editorials
After Second Patient Death, Duchenne Muscular Dystrophy Communities Want Answers About Elevidys Gene Therapy
Press Releases
Genethon Reports Results of GNT0004 Gene Therapy Clinical Trial: Permanent Decrease in CK Levels of More Than 75%
DMD
Micro Dystrophin: 5 Critical Questions Everyone Is Thinking About
DMD
The Dystrophin Gene: Function, Disorders, and Therapeutic Advances
Press Releases
Genethon CEO Frederic Revah Announces GNT0004 Gene Therapy Will Provide Amazing Results for DMD (Duchenne Muscular Dystrophy)
Press Releases
Biophytis’ BIO101 Therapy for Treatment of Sarcopenia Could Bring Hope to Duchenne Muscular Dystrophy Patients
Editorials
Clinical Trials Review of Elevidys Gene Therapy: Is Elevidys Cost Worthy?
Editorials
The Challenge of Getting DMD Gene Therapy: Is Geography Destiny?
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Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy
DMD Warrior
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December 26, 2024
Must Read
Editorials
Del-zota (EXPLORE44) Provides Nearly 30% Normal Dystrophin Production in Patients Amenable to Exon 44 Skipping
Press Releases
Belief BioMed BBM-D101 Gene Therapy Receives IND Clearance by National Medical Products Administration (NMPA)
Editorials
Dr. Aravindhan Veerapandiyan, a neurologist at Arkansas Children’s Hospital, Reviews RGX-202 Gene Therapy Study