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Press Releases
Satellos submits IND to FDA for Phase 2 SAT-3247 Clinical Trial in Duchenne Muscular Dystrophy
SAT-3247
Press Releases
Belief BioMed Announced Successful Completion of First Dose of BBM-D101 Gene Therapy
Research
Solid Biosciences Initiates Phase 3 Clinical Trial of SGT-003 Gene Therapy (IMPACT DUCHENNE) in Ambulant Males
Research
GNR-097: Duchenne Gene Therapy Phase 1/2 Study Started by Generium
Research
Genethon to Launch Pivotal Trial in Europe of GNT0004 a Low-Dose Microdystrophin Gene Therapy for Duchenne Muscular Dystrophy
Research
INS1201 Gene Therapy Phase 1 Clinical Trial Begins
Research
BBM-D101 Gene Therapy Phase 1/2 Clinical Trial Begins
Research
RGX-202 Gene Therapy Phase 3 Clinical Trial Begins
Press Releases
Edgewise Therapeutics Reports Positive Results on Sevasemten Program for Becker and Duchenne Muscular Dystrophies
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Popular
Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy
DMD Warrior
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December 26, 2024
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Editorials
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Does My Child Have Duchenne Muscular Dystrophy (DMD)?
Research
ELEVIDYS ENHANCE Study: A Phase 4 Trial Begins to Evaluate Safety and Effectiveness in Duchenne Muscular Dystrophy
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