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Latest Posts
Editorials
7 Breakthrough DMD Research Programs That Could Transform Duchenne Treatment in 2026
Press Releases
Dyne Therapeutics Announces U.S. FDA Acceptance of Biologics License Application (BLA) for Z-Rostudirsen, an Exon 51 Skipping Therapy for Duchenne Muscular Dystrophy (DMD)
Press Releases
Santhera Expands Biomedica Agreement to Extend AGAMREE (Vamorolone) Distribution Across Central Asia and the Caucasus
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DMD Warrior
Research
Stitch RNA: New Method for Duchenne Gene Therapies
Press Releases
Solid Biosciences Plans to Request a Meeting with the FDA in mid-2025 to Discuss Potential Accelerated Approval Pathways for SGT-003
Press Releases
GenAssist Announces FDA Approval of New Drug Application for GEN6050X Exon 50 Skipping Therapy
Press Releases
PepGen Temporarily Pauses Exon 51 Skipping Study
Press Releases
Capricor Therapeutics Announces FDA Acceptance and Priority Review of its Biologics License Application for Deramiocel to Treat Duchenne Muscular Dystrophy
Research
AlltRNA’s Engineered tRNA Technology Could Offer Hope for Nonsense Mutations
Press Releases
European Clinical Trial Map Launched
Research
Nanoparticles Used as Vehicle to Deliver MicroRNAs to Cells and Treat Duchenne Muscular Dystrophy
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Latest Posts
Editorials
7 Breakthrough DMD Research Programs That Could Transform Duchenne Treatment in 2026
Press Releases
Dyne Therapeutics Announces U.S. FDA Acceptance of Biologics License Application (BLA) for Z-Rostudirsen, an Exon 51 Skipping Therapy for Duchenne Muscular Dystrophy (DMD)
Press Releases
Santhera Expands Biomedica Agreement to Extend AGAMREE (Vamorolone) Distribution Across Central Asia and the Caucasus
DMD
Creatine Kinase Level in Duchenne Muscular Dystrophy: Normal Ranges, High CK Levels, Diagnosis, Blood Tests & FAQs
Don't Miss
Care Guidelines
Calcium in Duchenne Muscular Dystrophy: Mechanisms, Risks, and Treatment Insights
Editorials
Why CK, AST, and ALT Data Matter More Than Videos in Duchenne Gene Therapy
DMD
Does My Child Have Duchenne Muscular Dystrophy (DMD)?
Research
ELEVIDYS ENHANCE Study: A Phase 4 Trial Begins to Evaluate Safety and Effectiveness in Duchenne Muscular Dystrophy
Care Guidelines
Guide to DMD for Parents and Teachers at School: A Complete Guide for Safety, Learning, Friendship and Inclusion
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