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We do not want children to die from a disease that can be cured. We want to give hope to families and ensure that all children with DMD are treated and regain their health.

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Russia-Based Circle of Kindness Foundation Announces 18% Price Cut for Elevidys Gene Therapy

Press Releases 0
According to the Foundation's press office, "as a result...

Satellos Prepares to Launch Phase 2 Clinical Study of SAT-3247 for the Treatment of Duchenne Muscular Dystrophy

Research 0
Satellos Bioscience, a clinical-stage biotechnology company focused on developing...

Del-zota (EXPLORE44) Provides Nearly 30% Normal Dystrophin Production in Patients Amenable to Exon 44 Skipping

Editorials 0
A phase 1/2 EXPLORE44 study (NCT05670730) is now being...

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Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy

Approved Treatments 5
A genetic condition known as Duchenne muscular dystrophy (DMD)...

What is Duvyzat (Givinostat)?

Approved Treatments 1
For individuals with Duchenne muscular dystrophy (DMD), adults and...

Potential Upcoming New Gene Therapies for Duchenne Muscular Dystrophy

Research 2
The results of new gene therapy studies for Duchenne...

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