Home
Duchenne
Categories
Care Guidelines
Press Releases
Approved Therapies
Researches
Editorials
Family Stories
Our Tools
Exon Check Tool
Clinical Trials
Active Studies
Trial Statistics
Trials Map
Pipeline
Search
About Us
Contact
APPs
Privacy Policy
type here...
Search
Instagram
Facebook
Home
Duchenne
Duchenne MD
What is Duchenne?
Genetic Causes
Creatine Kinase (CK)
Genetic Testing
Prenatal Testing
Becker MD
DMD vs BMD
NSAA Assessment
Genetic
Genetic Counseling
Dystrophin Gene
Genetic Variants
Exon Deletion
Duchenne Carriers
Nucleotides in DMD
Isoforms in DMD
What is Exon Skipping
Care Guidelines
Newly Diagnosed
Neuromuscular Team
Respiratory Devices
BiPAP Machine
Ankle Foot Orthosis
Rhabdomyolysis
Power Wheelchair
Traveling with DMD
Health Guidelines
Psychological Support in DMD
Nutrition in DMD
Nutraceuticals
Respiratory Health
Dental Health
Surgery & Anesthesia
Swallowing Difficulty
Steroids (Cortisone)
Categories
Care Guidelines
Press Releases
Approved Therapies
Researches
Editorials
Family Stories
Our Tools
Exon Check Tool
Clinical Trials
Active Studies
Trial Statistics
Trials Map
Pipeline
WhatsAPP
Facebook
Instagram
X
Youtube
Latest Posts
Editorials
The Systemic Failure of DMD Associations: Why Duchenne Patients Are Still Waiting
Editorials
In Which Countries Is Elevidys Approved? Is Elevidys Approved In Europe?
Press Releases
Exegenesis Bio and Modalis Collaborate to Advance MDL-201 for Duchenne Muscular Dystrophy
Articles by:
Can Ekinci
Press Releases
Givinostat’s Exclusive Distribution Agreement in 17 Central and Eastern European Countries, Including the Baltic States, has been Announced by Italfarmaco and Medis
Press Releases
Biophytis’ BIO101 Therapy for Treatment of Sarcopenia Could Bring Hope to Duchenne Muscular Dystrophy Patients
Press Releases
Eteplirsen (Exondys 51) Treatment Significantly Slows Heart Function Decline in Duchenne Muscular Dystrophy
Research
Significant Improvements Seen in 3 Children Receiving Dystrogen Therapeutics’ DT-DEC01 Cell Therapy
Press Releases
Capricor Therapeutics Announces Positive Data Demonstrating Long-Term Efficacy of Deramiocel for the Treatment of Duchenne Muscular Dystrophy
Press Releases
ITF Therapeutics LLC Presents Long-Term Data of DUVYZAT™ (givinostat) for Treatment of Duchenne Muscular Dystrophy at MDA Clinical and Scientific Conference
Press Releases
Avidity Biosciences Announces Positive Topline Del-zota Data Showing Consistent, Statistically Significant Improvements in Dystrophin
Press Releases
Roche to Share Ongoing Work on Elevidys Gene Therapy at Muscular Dystrophy Association (MDA) 2025 Conference
1
...
35
36
37
...
47
Page 36 of 47
Latest Posts
Editorials
The Systemic Failure of DMD Associations: Why Duchenne Patients Are Still Waiting
Editorials
In Which Countries Is Elevidys Approved? Is Elevidys Approved In Europe?
Press Releases
Exegenesis Bio and Modalis Collaborate to Advance MDL-201 for Duchenne Muscular Dystrophy
Research
Tevard’s tRNA Therapy Targets Nonsense Mutations to Restore Full-Length Dystrophin in DMD
Don't Miss
Press Releases
Elixirgen and Nippon Shinyaku Partner on Full-Length Dystrophin Therapy for Duchenne
Press Releases
REGENXBIO Completes RGX-202 Confirmatory Study for Duchenne Muscular Dystrophy
Care Guidelines
DMD Circumcision Guide: Safety Precautions, Anesthesia, and Aftercare
Editorials
If Elevidys Works for Duchenne Muscular Dystrophy, Why Is Sarepta’s Stock Falling? What Families Need to Know Before Choosing Gene Therapy
Press Releases
GEn1E Lifesciences and GEn-1123: A New Precision Medicine Approach for Duchenne Muscular Dystrophy (DMD)
EN
AR
ZH
FR
DE
HI
RU
PT
ES
TR