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Duchenne MD
What is Duchenne?
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Latest Posts
Editorials
The Systemic Failure of DMD Associations: Why Duchenne Patients Are Still Waiting
Editorials
In Which Countries Is Elevidys Approved? Is Elevidys Approved In Europe?
Press Releases
Exegenesis Bio and Modalis Collaborate to Advance MDL-201 for Duchenne Muscular Dystrophy
Articles by:
Can Ekinci
Press Releases
U.S. Department of Defense Announces Duchenne Muscular Dystrophy Research Programs and Funding Opportunities for Fiscal Year 2025
Press Releases
Three Ongoing Clinical Trials of Elevidys Gene Therapy Temporarily Halted in Europe
Research
Keros Therapeutics Announces Initial Topline Results from the Phase 1 Clinical Trial of KER-065 in Healthy Volunteers
Research
Upcoming Exon 51 Skipping Therapies for the Treatment of Duchenne Muscular Dystrophy
Research
Shanghai Jiao Tong University School of Medicine Begins Clinical Trials of LE051 Exon 51 Skipping Therapy
Press Releases
Translarna (Ataluren) Rejected by EMA: Marketing Authorization Not Renewed
Research
Fn14 Protein May Protect Muscle Stem Cells, Offering Promise for Development of Duchenne Treatments
Editorials
During Wave, Dyne, Regenxbio, Genethon and Others Plan to File FDA Application, Potential Safety Issues in Duchenne Worry Patients
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Latest Posts
Editorials
The Systemic Failure of DMD Associations: Why Duchenne Patients Are Still Waiting
Editorials
In Which Countries Is Elevidys Approved? Is Elevidys Approved In Europe?
Press Releases
Exegenesis Bio and Modalis Collaborate to Advance MDL-201 for Duchenne Muscular Dystrophy
Research
Tevard’s tRNA Therapy Targets Nonsense Mutations to Restore Full-Length Dystrophin in DMD
Don't Miss
Press Releases
Elixirgen and Nippon Shinyaku Partner on Full-Length Dystrophin Therapy for Duchenne
Press Releases
REGENXBIO Completes RGX-202 Confirmatory Study for Duchenne Muscular Dystrophy
Care Guidelines
DMD Circumcision Guide: Safety Precautions, Anesthesia, and Aftercare
Editorials
If Elevidys Works for Duchenne Muscular Dystrophy, Why Is Sarepta’s Stock Falling? What Families Need to Know Before Choosing Gene Therapy
Press Releases
GEn1E Lifesciences and GEn-1123: A New Precision Medicine Approach for Duchenne Muscular Dystrophy (DMD)
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