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Latest Posts
Research
Sarcomatrix Plans First Human Trial of S-969 for Duchenne Muscular Dystrophy in 2027
Editorials
7 Breakthrough DMD Research Programs That Could Transform Duchenne Treatment in 2026
Press Releases
Dyne Therapeutics Announces U.S. FDA Acceptance of Biologics License Application (BLA) for Z-Rostudirsen, an Exon 51 Skipping Therapy for Duchenne Muscular Dystrophy (DMD)
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DMD Warrior
Research
WVE-N531 Exon Skipping Therapy Phase 2 Clinical Trial Begins for Duchenne Muscular Dystrophy
Press Releases
Genethon Confirms 2-Year Efficacy in Duchenne Muscular Dystrophy Patients Treated With Its Low Dose Micro-Dystrophin Gene Therapy (GNT0004)
Press Releases
Santhera Secures Agreement with Biomedica for the Distribution of AGAMREE (Vamorolone) in Russia
Press Releases
SonoThera Presents New Data at ESGCT 2025 Demonstrating Expression of Full-Length Human Dystrophin Using Targeted, Ultrasound-Mediated Delivery to Treat Duchenne Muscular Dystrophy
Press Releases
New Data Presented on Duvyzat (Givinostat) for Treatment of Duchenne Muscular Dystrophy at 2025 World Muscle Society Congress
Press Releases
Form Bio and Cure Rare Disease Partner to Accelerate Genetic Medicine Development, Advancing CRD’s Duchenne Muscular Dystrophy Program
Approved Therapies
Zydus Lifesciences Receives FDA Approval for Deflazacort to Treat DMD
Editorials
Could Axolotl’s Self Regenerative Ability Be Effective in Treating Duchenne Muscular Dystrophy?
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Latest Posts
Research
Sarcomatrix Plans First Human Trial of S-969 for Duchenne Muscular Dystrophy in 2027
Editorials
7 Breakthrough DMD Research Programs That Could Transform Duchenne Treatment in 2026
Press Releases
Dyne Therapeutics Announces U.S. FDA Acceptance of Biologics License Application (BLA) for Z-Rostudirsen, an Exon 51 Skipping Therapy for Duchenne Muscular Dystrophy (DMD)
Press Releases
Santhera Expands Biomedica Agreement to Extend AGAMREE (Vamorolone) Distribution Across Central Asia and the Caucasus
Don't Miss
Care Guidelines
Constipation in Duchenne Muscular Dystrophy: Causes, Symptoms & Treatment
Care Guidelines
Calcium in Duchenne Muscular Dystrophy: Mechanisms, Risks, and Treatment Insights
Editorials
Why CK, AST, and ALT Data Matter More Than Videos in Duchenne Gene Therapy
DMD
Does My Child Have Duchenne Muscular Dystrophy (DMD)?
Research
ELEVIDYS ENHANCE Study: A Phase 4 Trial Begins to Evaluate Safety and Effectiveness in Duchenne Muscular Dystrophy
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