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We do not want children to die from a disease that can be cured. We want to give hope to families and ensure that all children with DMD are treated and regain their health.

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Latest Articles

FDA Allows Expanded Enrollment in Signature Biologics’ DMD Cell Therapy Study

Press Releases August 11, 2026 0

Signature Biologics has announced that the U.S. Food and...

Exon 45 Skipping in DMD: Deletions and Mutations That May Be Eligible

DMD August 10, 2026 0

As of recent years, exon skipping has emerged as...

Mutations and Deletions Amenable to Exon 44 Skipping Therapies for Duchenne Muscular Dystrophy

DMD August 9, 2026 0

Deletions amenable to exon 44 skipping are specific genetic...

Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy

Approved Therapies December 26, 2024 0

A genetic condition known as Duchenne muscular dystrophy (DMD)...

Potential Upcoming New Gene Therapies for Duchenne Muscular Dystrophy

Editorials April 10, 2026 0

The landscape of potential new gene therapies for Duchenne...

The Brutal Truth: Why Duchenne Muscular Dystrophy Treatment Costs Are Out of Control

Editorials April 6, 2026 0

The duchenne muscular dystrophy treatment cost has become one...

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Must Read

Elevidys Under Scrutiny: A Candid Interview with the Turkish Representative of DMDWarrioR on Cost, Effectiveness, and Ethics

Psychological Support in DMD: Coping Strategies for Families and Children After Diagnosis

Vamorolone (Agamree) Rejected by INESSS: When Cost Takes Priority Over Compassion in DMD Care