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We do not want children to die from a disease that can be cured. We want to give hope to families and ensure that all children with DMD are treated and regain their health.

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Latest Articles

Do Social Media Hashtag Campaigns Really Help DMD Associations Improve Access to Approved Treatments for DMD Families?

Editorials August 7, 2026 0

Every year, dozens of Duchenne muscular dystrophy (DMD) associations...

IPS HEART Aims to Restore Full-Length Dystrophin with Two Regenerative Cell Therapies for Duchenne Muscular Dystrophy

Press Releases August 6, 2026 0

IPS HEART has announced another important regulatory milestone after...

20 Important Things You Need to Know About DMD Genetic Testing

DMD August 1, 2026 0

DMD genetic testing for Duchenne muscular dystrophy involves analyzing...

Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy

Approved Therapies December 26, 2024 0

A genetic condition known as Duchenne muscular dystrophy (DMD)...

Potential Upcoming New Gene Therapies for Duchenne Muscular Dystrophy

Editorials April 10, 2026 0

The landscape of potential new gene therapies for Duchenne...

The Brutal Truth: Why Duchenne Muscular Dystrophy Treatment Costs Are Out of Control

Editorials April 6, 2026 0

The duchenne muscular dystrophy treatment cost has become one...

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Enlarged Calf Muscles in Duchenne Muscular Dystrophy: Causes, Symptoms & Treatment

Precision BioSciences Announced the Start of Phase 1/2a (FUNCTION-DMD) Study of PBGENE-DMD in Ambulatory Patients with Duchenne

PBGENE-DMD Gene Editing Therapy: Benefits, Eligibility, and FAQs