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NS-051/NCNP-04
NS-051/NCNP-04
Press Releases
FDA Grants Rare Pediatric Disease Designation to Nippon Shinyaku’s Exon 51 Skipping Study (NS-051/NCNP-04)
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Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy
DMD Warrior
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December 26, 2024
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DMD
Micro Dystrophin: 5 Critical Questions Everyone Is Thinking About
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SonoThera Ultrasound-Mediated Delivery Method Can Deliver Full-Length Dystrophin to Cells
Press Releases
Scribe Therapeutics and Prevail Therapeutics to Share In Vivo CRISPR-based Genome Editing Data at ASGCT 2025