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Duchenne MD
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Japan
Japan
Press Releases
Nxera Pharma Licenses Japan and Select Asia-Pacific Rights to Vamorolone for Duchenne Muscular Dystrophy from Santhera Pharmaceuticals
Press Releases
Italfarmaco and JCR Pharmaceuticals Announce Commercialisation Agreement for Duvyzat (Givinostat) in Japan and Strategic Collaboration in Rare Disease
Press Releases
Dyne Therapeutics Receives Orphan Drug Designation in Japan for DYNE-251 in Duchenne Muscular Dystrophy
Press Releases
Sarepta Therapeutics Announces Approval in Japan of ELEVIDYS, a Gene Therapy to Treat Duchenne Muscular Dystrophy
Research
Nippon Shinyaku Releases First Clinical Trial (First in Human) of Brogidirsen NS-089/NCNP-02 for the Treatment of Duchenne
Popular
Frequently Asked Questions About Elevidys Used for DMD
Can Ekinci
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August 21, 2026
Must Read
Research
Del-Zota SAFARI44 Phase 3 Trial: A New Exon 44 Skipping Study for Duchenne Muscular Dystrophy
Press Releases
RGX-202 Duchenne Gene Therapy Shows NSAA Improvement and Microdystrophin Expression — But Important Biomarker Data Missing
Editorials
CRISPR GuideX Tool: hfCas12Max in CRISPR-Based Therapeutics
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