Exon Skipping

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We do not want children to die from a disease that can be cured. We want to give hope to families and ensure that all children with DMD are treated and regain their health.

Latest Articles

South Korean Trending News: Father Walks 740 km for Daughter with Duchenne Muscular Dystrophy

Family Stories January 21, 2025 0

Father Joseph Jeon, who is trying to raise funds...

Elevidys Gene Therapy has Arrived in Brazil and Could Cost up to 20 Million Brazilian Reais

DMD January 21, 2025 0

There is no definitive treatment for Duchenne muscular dystrophy...

Next Generation Exon Skipping Therapies Developed for the Treatment of Duchenne Muscular Dystrophy

Research January 16, 2025 2

Next generation exon skipping therapies for Duchenne Muscular Dystrophy...

Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy

DMD December 26, 2024 1

A genetic condition known as Duchenne muscular dystrophy (DMD)...

Capricor Therapeutics Submits Application for Treatment of DMD Cardiomyopathy

Research October 10, 2024 0

Capricor Therapeutics, a biotechnology company developing transformative cell and...

Cures of Duchenne (List of All Researches)

Research September 20, 2024 3

Dystrophin Gene Therapy MechanismCompanyDrugStatus Micro-dystrophin Gene Replacement Sarepta TherapeuticsElevidys/SRP-9001ApprovedMicro-dystrophin Gene ReplacementPfizerPF-06939926DiscontinuedMicro-dystrophin Gene...

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Must Read

What are The Differences Between Duchenne Muscular Dystrophy and Becker Muscular Dystrophy?

First Girl in the World to Receive Elevidys Gene Therapy: Raniya Scott

University of Miami Health System and Holtz Children’s Hospital Physicians Evaluated the Effectiveness of ELEVIDYS