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Exon 44
Exon 44
Editorials
Del-zota (EXPLORE44) Provides Nearly 30% Normal Dystrophin Production in Patients Amenable to Exon 44 Skipping
Press Releases
Avidity Biosciences Announces Positive Topline Del-zota Data Showing Consistent, Statistically Significant Improvements in Dystrophin
Press Releases
Entrada Therapeutics Receives FDA Approval to Begin Clinical Trial of ENTR-601-44 Exon Skipping Treatment
Research
Upcoming Exon 44 Skipping Therapies for the Treatment of Duchenne Muscular Dystrophy
Press Releases
Entrada Therapeutics Receives UK Authorization to Begin ELEVATE-44-201
Research
Nippon Shinyaku Releases First Clinical Trial (First in Human) of Brogidirsen NS-089/NCNP-02 for the Treatment of Duchenne
Popular
Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy
DMD Warrior
-
December 26, 2024
Must Read
Press Releases
Three Ongoing Clinical Trials of Elevidys Gene Therapy Temporarily Halted in Europe
Research
Keros Therapeutics Announces Initial Topline Results from the Phase 1 Clinical Trial of KER-065 in Healthy Volunteers
Research
Upcoming Exon 51 Skipping Therapies for the Treatment of Duchenne Muscular Dystrophy