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Exon 44 Skipping
Exon 44 Skipping
Research
Upcoming Exon 44 Skipping Therapies for the Treatment of Duchenne Muscular Dystrophy
Research
Entrada Therapeutics Receives UK Authorization to Begin ELEVATE-44-201
Research
Nippon Shinyaku Releases First Clinical Trial (First in Human) of Brogidirsen NS-089/NCNP-02 for the Treatment of Duchenne
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Research
39
DMD
37
Approved Treatments
7
Family Stories
3
Must Read
Research
Insmed’s Gene Therapy (INS1201) Poised to Challenge Duchenne Muscular Dystrophy (DMD)
Research
Solid Biosciences Releases Information on Clinical Trial for SGT-003 Gene Therapy
Approved Treatments
NICE Final Guidance for AGAMREE (Vamorolone) as a Treatment for Duchenne Muscular Dystrophy Is Positive for Santhera