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ELEVATE-44-201
ELEVATE-44-201
Research
Entrada Therapeutics Receives UK Authorization to Begin ELEVATE-44-201
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Research
39
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37
Approved Treatments
7
Family Stories
3
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Research
Insmed’s Gene Therapy (INS1201) Poised to Challenge Duchenne Muscular Dystrophy (DMD)
Research
Solid Biosciences Releases Information on Clinical Trial for SGT-003 Gene Therapy
Approved Treatments
NICE Final Guidance for AGAMREE (Vamorolone) as a Treatment for Duchenne Muscular Dystrophy Is Positive for Santhera