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We do not want children to die from a disease that can be cured. We want to give hope to families and ensure that all children with DMD are treated and regain their health.

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Latest Articles

If Elevidys Works for Duchenne Muscular Dystrophy, Why Is Sarepta’s Stock Falling? What Families Need to Know Before Choosing Gene Therapy

Editorials June 12, 2026 0

Few Duchenne muscular dystrophy (DMD) treatments have generated as...

GEn1E Lifesciences and GEn-1123: A New Precision Medicine Approach for Duchenne Muscular Dystrophy (DMD)

Press Releases June 10, 2026 0

The U.S. Food and Drug Administration (FDA) has granted...

Pain Management in Duchenne Muscular Dystrophy: A Parent’s Guide to Helping Your Child Live More Comfortably

Care Guidelines June 5, 2026 0

Living with Duchenne muscular dystrophy (DMD) involves far more...

Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy

Approved Therapies December 26, 2024 4

A genetic condition known as Duchenne muscular dystrophy (DMD)...

Potential Upcoming New Gene Therapies for Duchenne Muscular Dystrophy

Editorials April 10, 2026 9

The landscape of potential new gene therapies for Duchenne...

The Brutal Truth: Why Duchenne Muscular Dystrophy Treatment Costs Are Out of Control

Editorials April 6, 2026 2

The duchenne muscular dystrophy treatment cost has become one...

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