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Ifetroban
Research
Cumberland Pharmaceuticals Announces Fantastic Results from Phase 2 FIGHT Duchenne Trial in DMD Heart Disease
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Research
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37
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7
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Must Read
Research
Insmed’s Gene Therapy (INS1201) Poised to Challenge Duchenne Muscular Dystrophy (DMD)
Research
Solid Biosciences Releases Information on Clinical Trial for SGT-003 Gene Therapy
Approved Treatments
NICE Final Guidance for AGAMREE (Vamorolone) as a Treatment for Duchenne Muscular Dystrophy Is Positive for Santhera