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Gene Editing
Gene Editing
Research
PBGENE-DMD Enters Clinical Trials: First Patient Dosed in Duchenne Gene-Editing Study
Research
Precision BioSciences Announced the Start of Phase 1/2a (FUNCTION-DMD) Study of PBGENE-DMD in Ambulatory Patients with Duchenne
Editorials
Potential Upcoming New Gene Therapies for Duchenne Muscular Dystrophy
Press Releases
Precision BioSciences Receives U.S. FDA Clearance of Investigational New Drug Application for First-in-Class PBGENE-DMD for Treatment of Duchenne Muscular Dystrophy
Press Releases
Precision BioSciences Anticipates Beginning Patient Dosing for Duchenne Muscular Dystrophy in The Early Second Quarter of 2026
Press Releases
Precision BioSciences Highlights New Preclinical Data for PBGENE-DMD for the Treatment of Duchenne Muscular Dystrophy
Press Releases
Precision BioSciences Receives FDA Rare Pediatric Disease Designation for PBGENE-DMD for the Treatment of Duchenne Muscular Dystrophy
Press Releases
Precision BioSciences PBGENE-DMD Restores Production of Nearly Full-Length Dystrophin Protein
Press Releases
Scribe Therapeutics and Prevail Therapeutics to Share In Vivo CRISPR-based Genome Editing Data at ASGCT 2025
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Popular
Frequently Asked Questions About Elevidys Used for DMD
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August 21, 2026
Must Read
Editorials
CRISPR GuideX Tool: hfCas12Max in CRISPR-Based Therapeutics
Care Guidelines
Breathing Exercises in Duchenne Muscular Dystrophy: Respiratory Therapy, Pulmonary Care & Lung Support
Research
BioMarin Launches BMN 351 Exon 51 Skipping Therapy Phase 2 Clinical Trial for Duchenne Muscular Dystrophy
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