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Gene Editing
Gene Editing
Press Releases
Scribe Therapeutics and Prevail Therapeutics to Share In Vivo CRISPR-based Genome Editing Data at ASGCT 2025
Press Releases
Precision BioSciences Presents Preclinical Efficacy and Durability Data on PBGENE-DMD for the Treatment of Duchenne Muscular Dystrophy (DMD) at the 2025 Muscular Dystrophy Association...
Research
Hydrogel Delivery System Holds Potential for Cell-Based Therapy of Duchenne Muscular Dystrophy
Research
A Novel “Mini-CRISPR” Could Be More Successful at Editing the Dystrophin Gene
Press Releases
Will Genethon and Eukarÿs Partnership Reduce the Cost of Gene Therapies?
Research
Insmed’s Gene Therapy (INS1201) Poised to Challenge Duchenne Muscular Dystrophy (DMD)
Research
Solid Biosciences Releases Information on Clinical Trial for SGT-003 Gene Therapy
Research
Potential Upcoming New Gene Therapies for Duchenne Muscular Dystrophy
Editorials
Duchenne Muscular Dystrophy: Treatment & Cost
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Popular
Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy
DMD Warrior
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December 26, 2024
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Press Releases
Entrada Therapeutics Receives Authorization in the United Kingdom to Initiate ELEVATE-45-201
DMD
Explore Of 5 Phases In Drug Development
Press Releases
Regenxbio Reports Positive Biomarker Data From Affinity Duchenne Trial Of Rgx-202 Gene Therapy