欧洲暂停三项正在进行的 Elevidys 基因疗法临床试验

Three ongoing clinical trials of ELEVIDYS (delandistrogene moxeparvovec-rokl), a gene therapy developed by Sarepta and marketed by Roche, have...

Keros Therapeutics 公布 KER-065 在健康志愿者中进行的 1 期临床试验的初步结果

Keros Therapeutics, a clinical-stage biopharmaceutical company focused on developing and commercializing novel therapeutics to treat a wide range of...

杜氏肌营养不良症 (DMD) 外显子 51 跳跃疗法:有希望的治疗方法和临床试验

Duchenne Exon 51 skipping therapies are innovative treatments aimed at addressing the genetic mutation responsible for Duchenne muscular dystrophy...