Metagenomi’s New CRISPR System (VK CAST) Enables Large Gene Integration
Metagenomi, a precision genetic medicines company committed to developing curative therapeutics for patients using its proprietary gene editing toolbox, today announced a publication in...
Hydrogel Delivery System Holds Potential for Cell-Based Therapy of Duchenne Muscular Dystrophy
In a mouse model of muscular dystrophy, researchers in the UK announced a clinically applicable transplantation method that uses CRISPR-corrected human myogenic cells in...
OligomicsTx Gene Therapy Study Shows Promise in Treating Duchenne Muscular Dystrophy
The University of Alberta researchers develop a molecule that bypasses genetic mutation to restore a crucial muscle-repairing protein. Learn more about OligomicsTx Gene Therapy...
Stitch RNA: New Method for Duchenne Gene Therapies
The Stitch RNA (StitchR) method could accelerate the development of new drugs that could significantly treat Duchenne Muscular Dystrophy.
Loss of the DNA code that...
AlltRNA’s Engineered tRNA Technology Could Offer Hope for Nonsense Mutations
Regardless of the impacted protein, Alltrna is creating designed tRNA medications that can read through premature termination codons and resume production of the impacted...