Significant Improvements Seen in 3 Children Receiving Dystrogen Therapeutics’ DT-DEC01 Cell Therapy
In non-ambulatory individuals with Duchenne muscular dystrophy (DMD), DT-DEC01 (Dystrogen Therapeutics), an experimental dystrophin expressing chimeric (DEC) cell treatment, was found to be safe...
Researchers in Madrid Make Important Strides in the Cure of Duchenne Muscular Dystrophy with Nanoparticles
The Community of Madrid has achieved significant progress in therapy for Duchenne muscular dystrophy, a degenerative disease for which there is still no cure....
Metagenomi’s New CRISPR System (VK CAST) Enables Large Gene Integration
Metagenomi, a precision genetic medicines company committed to developing curative therapeutics for patients using its proprietary gene editing toolbox, today announced a publication in...
Hydrogel Delivery System Holds Potential for Cell-Based Therapy of Duchenne Muscular Dystrophy
In a mouse model of muscular dystrophy, researchers in the UK announced a clinically applicable transplantation method that uses CRISPR-corrected human myogenic cells in...
OligomicsTx Gene Therapy Study Shows Promise in Treating Duchenne Muscular Dystrophy
The University of Alberta researchers develop a molecule that bypasses genetic mutation to restore a crucial muscle-repairing protein. Learn more about OligomicsTx Gene Therapy...