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Press Releases
Capricor Therapeutics Announces BMD Orphan Drug Designation and DMD Program Regulatory Development for Deramiocel (CAP-1002)
Press Releases
Capricor Therapeutics Announces Completion of Mid-Cycle Review Meeting with FDA on Deramiocel for the Treatment of Duchenne Muscular Dystrophy Cardiomyopathy
DMD
Explore Of 5 Phases In Drug Development
Press Releases
Solid Biosciences Plans to Request a Meeting with the FDA in mid-2025 to Discuss Potential Accelerated Approval Pathways for SGT-003
Press Releases
GenAssist Announces FDA Approval of New Drug Application for GEN6050X Exon 50 Skipping Therapy
Press Releases
Capricor Therapeutics Announces FDA Acceptance and Priority Review of its Biologics License Application for Deramiocel to Treat Duchenne Muscular Dystrophy
Editorials
Clinical Trials Review of Elevidys Gene Therapy: Is Elevidys Cost Worthy?
Approved Treatments
FDA-Approved Treatments for DMD (Duchenne Muscular Dystrophy)
Press Releases
FDA Grants Rare Pediatric Disease Designation to Nippon Shinyaku’s Exon 51 Skipping Study (NS-051/NCNP-04)
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Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy
DMD Warrior
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December 26, 2024
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Press Releases
Dyne Therapeutics Receives European Medicines Agency (EMA) Orphan Drug Designation for DYNE-251 in Duchenne Muscular Dystrophy
Press Releases
Agamree (vamorolone) will be Covered in Slovenia by the Slovenian Health Insurance Fund
Press Releases
Russia-Based Circle of Kindness Foundation Announces 18% Price Cut for Elevidys Gene Therapy