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Satellos Receives FDA Fast Track Designation for SAT-3247 in Duchenne Muscular Dystrophy

REGENXBIO Completes RGX-202 Confirmatory Study for Duchenne Muscular Dystrophy

Medera’s Gene Therapy for DMD Cardiomyopathy Gains Momentum with FDA Fast Track Designation

Approved Therapies

Approved Treatments for Duchenne Muscular Dystrophy

Solid Biosciences Aligns With FDA on SGT-003 Phase 3 Trial Design for Duchenne Muscular Dystrophy Gene Therapy

Satellos Receives FDA and International Clearance to Commence Pediatric Phase 2 Testing of SAT-3247 for Duchenne Muscular Dystrophy

Why Does the FDA Approve DMD Therapies That Fail in Clinical Trials?

Biologics License Application (BLA): A Complete Guide to the FDA Approval Process

Avidity Biosciences Announces Positive Pre-BLA Meeting with U.S. FDA for del-zota in DMD44 with a Submission Planned for Q1 2026

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Frequently Asked Questions About Elevidys Used for DMD

Can Ekinci - August 21, 2026

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Del-Zota SAFARI44 Phase 3 Trial: A New Exon 44 Skipping Study for Duchenne Muscular Dystrophy

RGX-202 Duchenne Gene Therapy Shows NSAA Improvement and Microdystrophin Expression — But Important Biomarker Data Missing

CRISPR GuideX Tool: hfCas12Max in CRISPR-Based Therapeutics

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