Лечения Дюшенна (список всех исследований)
Dystrophin Gene Therapy
MechanismCompanyDrugStatus
Micro-dystrophin Gene Replacement Sarepta TherapeuticsElevidys/SRP-9001ApprovedMicro-dystrophin Gene ReplacementPfizerPF-06939926DiscontinuedMicro-dystrophin Gene ReplacementGenethon (Sarepta)GNT-0004ClinicalMicro-dystrophin Gene ReplacementRegenxBioRGX-202ClinicalMicro-dystrophin Gene ReplacementSolid BiosciencesSGT-001ClinicalMicro-dystrophin Gene ReplacementSolid BiosciencesSGT-003ClinicalMicro-dystrophin Gene ReplacementBelief BioMedBBM-D101ClinicalMicro-dystrophin Gene ReplacementInsmedINS1201ClinicalMicro-dystrophin...