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Gene Therapy
Gene Therapy
Press Releases
Elevidys Gene Therapy has Arrived in Brazil and Could Cost up to 20 Million Brazilian Reais
Research
Insmed’s Gene Therapy (INS1201) Poised to Challenge Duchenne Muscular Dystrophy (DMD)
Research
Solid Biosciences Releases Information on Clinical Trial for SGT-003 Gene Therapy
Press Releases
Sarepta Reiterated Total Net Product Revenue of $3.0 Billion in 2025
Research
Potential Upcoming New Gene Therapies for Duchenne Muscular Dystrophy
Editorials
In Which Countries Is Elevidys Approved? Is Elevidys Approved In Europe?
Editorials
Duchenne Muscular Dystrophy: Treatment & Cost
Research
Is Duchenne Gene Therapy a Suitable Treatment Despite its Immunogenic Class Effect?
Research
New Research on Duchenne Muscular Dystrophy Protein Interactions Lead to More Targeted Therapies
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Popular
Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy
DMD Warrior
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December 26, 2024
Must Read
DMD
Micro Dystrophin: 5 Critical Questions Everyone Is Thinking About
Press Releases
SonoThera Ultrasound-Mediated Delivery Method Can Deliver Full-Length Dystrophin to Cells
Press Releases
Scribe Therapeutics and Prevail Therapeutics to Share In Vivo CRISPR-based Genome Editing Data at ASGCT 2025