First Girl in the World to Receive Elevidys Gene Therapy: Raniya Scott
When Raniya Scott was just two years old, her world changed with an unexpected diagnosis: Duchenne muscular dystrophy (DMD), a group of diseases that...
University of Miami Health System and Holtz Children’s Hospital Physicians Evaluated the Effectiveness of ELEVIDYS
University of Miami Health System and Holtz Children’s Hospital physicians are playing a major role in getting ELEVIDYS access.
The therapy delivers a functional micro-gene...
Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy
A genetic condition known as Duchenne muscular dystrophy (DMD) results in gradual muscle weakening. Boys are more likely to have DMD, with symptoms first...
What does DMD Warrior mean?
A DMD Warrior (aka Duchenne Warrior) is a term used to describe individuals who are diagnosed with Duchenne muscular dystrophy, a rare genetic disorder...
Does My Child Have Duchenne Muscular Dystrophy (DMD)?
When parents ponder the question, “Does My Child Have Duchenne Muscular Dystrophy (DMD)?” they often find themselves grappling with a whirlwind of emotions as...