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Clinical Trial
Clinical Trial
Research
Satellos Prepares to Launch Phase 2 Clinical Study of SAT-3247 for the Treatment of Duchenne Muscular Dystrophy
Research
Keros Therapeutics Announces Initial Topline Results from the Phase 1 Clinical Trial of KER-065 in Healthy Volunteers
Press Releases
PepGen Temporarily Pauses Exon 51 Skipping Study
Press Releases
Solid Biosciences Reports Positive Initial Clinical Data from Next-Generation Duchenne Gene Therapy Candidate SGT-003
Research
Nippon Shinyaku Releases First Clinical Trial (First in Human) of Brogidirsen NS-089/NCNP-02 for the Treatment of Duchenne
Popular
Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy
DMD Warrior
-
December 26, 2024
Must Read
Press Releases
Translarna (Ataluren) Rejected by EMA: Marketing Authorization Not Renewed
Editorials
DMD WarrioR’s Turkish Representative Shares His Views on Elevidys Gene Therapy: Is It Effective and Why Is It Expensive?
Research
Fn14 Protein May Protect Muscle Stem Cells, Offering Promise for Development of Duchenne Treatments