Clinical Trial

About us

We do not want children to die from a disease that can be cured. We want to give hope to families and ensure that all children with DMD are treated and regain their health.

Latest Articles

Plans for DYNE-101 in DM1 and DYNE-251 in DMD Are Announced by Dyne Therapeutics

Research January 10, 2025 0

Dyne Therapeutics announced positive clinical data for its therapies...

Nippon Shinyaku Releases First Clinical Trial (First in Human) of Brogidirsen NS-089/NCNP-02 for the Treatment of Duchenne

Research January 10, 2025 0

The National Center of Neurology and Psychiatry is announced...

What is Ataluren (Translarna)? What is Ataluren Used For?

Research January 9, 2025 0

Ataluren (Translarna) is an investigational drug used to delay...

Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy

DMD December 26, 2024 1

A genetic condition known as Duchenne muscular dystrophy (DMD)...

Capricor Therapeutics Submits Application for Treatment of DMD Cardiomyopathy

Research October 10, 2024 0

Capricor Therapeutics, a biotechnology company developing transformative cell and...

Cures of Duchenne (List of All Researches)

Research September 20, 2024 3

Dystrophin Gene Therapy MechanismCompanyDrugStatus Micro-dystrophin Gene Replacement Sarepta TherapeuticsElevidys/SRP-9001ApprovedMicro-dystrophin Gene ReplacementPfizerPF-06939926DiscontinuedMicro-dystrophin Gene...

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Must Read

Genetic Causes of Duchenne Muscular Dystrophy

CRISPR-Cas13 Could Accelerate Studies on RNA-Targeted Therapies

New Gene Therapy Study at Indiana University Offers Hope for Duchenne Muscular Dystrophy