Duchenne Muscular Dystrophy News

Entrada Therapeutics Begins Clinical Trials in Europe for Exon 44 and Exon 45 Skipping Therapies

Research DMD Warrior -

Entrada Therapeutics has officially launched clinical trials in Europe for its innovative exon skipping therapies targeting Exon 44 and...

Wellcome Trust Donates £10 Million to Treat Rare Diseases

Editorials DMD Warrior -

The new Synthetic Human Genome Project (SynHG) is receiving £10 million from Wellcome Trust to build the fundamental instruments,...

Edgewise Therapeutics Reports Positive Results on Sevasemten Program for Becker and Duchenne Muscular Dystrophies

Press Releases DMD Warrior -

Edgewise Therapeutics, a leading muscle disease biopharmaceutical company, today unveiled positive results in its sevasemten program for Becker and...

Precision BioSciences Receives FDA Rare Pediatric Disease Designation for PBGENE-DMD for the Treatment of Duchenne Muscular Dystrophy

Press Releases DMD Warrior -

Capricor Therapeutics Provides Regulatory Update on Deramiocel BLA for Duchenne Muscular Dystrophy

Press Releases DMD Warrior -

Cumberland’s Ifetroban Demonstrated a 5.4% Improvement Compared to Placebo-Treated Patients

Press Releases DMD Warrior -

What is Duvyzat (Givinostat)?

Approved Treatments DMD Warrior -

About us

We do not want children to die from a disease that can be cured. We want to give hope to families and ensure that all children with DMD are treated and regain their health.