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Duchenne Muscular Dystrophy
Duchenne Muscular Dystrophy
Press Releases
Plans for DYNE-101 in DM1 and DYNE-251 in DMD Are Announced by Dyne Therapeutics
Research
What is Ataluren (Translarna)? What is Ataluren Used For?
Press Releases
Avidity Biosciences Prepares for Three Rare Muscle Disease Programs’ 2025 BLA Submission and Commercialization
Press Releases
Percheron Disappointed in Avicursen (ATL1102) Study For Duchenne (DMD)
DMD
20 Important Things You Need to Know About DMD Genetic Testing
Research
Is Duchenne Gene Therapy a Suitable Treatment Despite its Immunogenic Class Effect?
Research
New Research on Duchenne Muscular Dystrophy Protein Interactions Lead to More Targeted Therapies
DMD
What are The Differences Between Duchenne Muscular Dystrophy and Becker Muscular Dystrophy?
Approved Treatments
Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy
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Popular
Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy
DMD Warrior
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December 26, 2024
Must Read
Press Releases
ITF Therapeutics LLC Presents Long-Term Data of DUVYZAT™ (givinostat) for Treatment of Duchenne Muscular Dystrophy at MDA Clinical and Scientific Conference
Press Releases
Avidity Biosciences Announces Positive Topline Del-zota Data Showing Consistent, Statistically Significant Improvements in Dystrophin
Press Releases
Roche to Share Ongoing Work on Elevidys Gene Therapy at Muscular Dystrophy Association (MDA) 2025 Conference